HomeTrialNCT04849741
🔬NCT04849741Phase 3ACTIVE NOT RECRUITING

A Study to Evaluate the Safety and Efficacy of Zilganersen (ION373) in Patients With Alexander Disease (AxD)

Study Summary

The purpose of this study is to evaluate the safety and efficacy of zilganersen (ION373) in improving or stabilizing gross motor function across the full range of affected domains in patients with AxD.

Interventions / Drugs
View on ClinicalTrials.gov ↗
Study Details
Enrollment54 participants
Primary Completion
Lead SponsorIonis Pharmaceuticals, Inc.
Data Retrieved2026-04-11 04:17:53.139432+00:00
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