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Agios Pharmaceuticals

AGIORare Disease
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Analyst Summary
✓ VERIFIED2026-04-11

Agios Pharmaceuticals (AGIO) is the lead sponsor of 11 active clinical trials listed on ClinicalTrials.gov[5], including 5 Phase 3[1], 4 Phase 2[2], 1 Phase 1[3], 1 Phase 4[4].

Trial NCT05144256[6] evaluates Mitapivat in Pediatric Pyruvate Kinase Deficiency with a target enrollment of 49 participants. Trial NCT04770779[7] evaluates Placebo Matching Mitapivat in Transfusion-dependent Alpha-Thalassemia with a target enrollment of 258 participants. Trial NCT05031780[8] evaluates Mitapivat in Sickle Cell Disease with a target enrollment of 286 participants.

AGIO has 6 Form 4 insider filings recorded at the SEC in the past 30 days[9].

Sources

  1. ClinicalTrials.gov (2026-04-11)
  2. ClinicalTrials.gov (2026-04-11)
  3. ClinicalTrials.gov (2026-04-11)
  4. ClinicalTrials.gov (2026-04-11)
  5. ClinicalTrials.gov (2026-04-11)
  6. ClinicalTrials.gov · NCT05144256 (2026-03-30)
  7. ClinicalTrials.gov · NCT04770779 (2026-03-30)
  8. ClinicalTrials.gov · NCT05031780 (2026-03-30)
  9. SEC EDGAR · 0001439222 (2026-04-11)
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Clinical Trials
11
NCT03481738Pyruvate Kinase Deficiency
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT03692052Thalassemia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04770753Non-Transfusion-dependent Alpha-Thalassemia, Non-Transfusion-dependent Beta-Thalassemia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04770779Transfusion-dependent Alpha-Thalassemia, Transfusion-dependent Beta-Thalassemia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05031780Sickle Cell Disease
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05144256Pediatric Pyruvate Kinase Deficiency, Pediatric Hemolytic Anemia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05175105Pediatric Pyruvate Kinase Deficiency, Pediatric Hemolytic Anemia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05490446Myelodysplastic Syndromes
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05777993Pyruvate Kinase Deficiency, Anemia, Hemolytic
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06924970Sickle Cell Disease
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07075640Healthy Participants
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
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Insider Activity
1
6 filings
Source ↗
sec_edgar · Retrieved 2026-04-11
Not financial advice. BiotechSigns profiles are AI-generated from verified public sources (ClinicalTrials.gov, SEC EDGAR) and are for informational purposes only. Always do your own due diligence before making investment decisions.
Score Breakdown
Score Trend
2026-04-132026-06-02
Signal Summary
PDUFA Dates0
Insider Filings1
Clinical Trials5
Data Provenance
cik1 verified
clinical trial11 verified
insider buy1 verified
trial count5 verified
Every claim backed by source URL from ClinicalTrials.gov or SEC EDGAR