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Alnylam Pharmaceuticals

ALNYRNAi Therapeutics
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Analyst Summary
✓ VERIFIED2026-04-11

Alnylam Pharmaceuticals (ALNY) is the lead sponsor of 22 active clinical trials listed on ClinicalTrials.gov[4], including 6 Phase 3[1], 5 Phase 2[2], 8 Phase 1[3].

Trial NCT06679946[5] evaluates Vutrisiran in Transthyretin Amyloidosis (ATTR) With Cardiomyopathy with a target enrollment of 700 participants. Trial NCT07223203[6] evaluates Nucresiran in Hereditary Transthyretin-Mediated Amyloidosis With Polyneuropathy with a target enrollment of 125 participants. Trial NCT07181109[7] evaluates Zilebesiran in High Risk Cardiovascular Disease with a target enrollment of 11000 participants.

ALNY has 1 Form 4 insider filing recorded at the SEC in the past 30 days[8].

Sources

  1. ClinicalTrials.gov (2026-04-11)
  2. ClinicalTrials.gov (2026-04-11)
  3. ClinicalTrials.gov (2026-04-11)
  4. ClinicalTrials.gov (2026-04-11)
  5. ClinicalTrials.gov · NCT06679946 (2026-02-20)
  6. ClinicalTrials.gov · NCT07223203 (2026-01-14)
  7. ClinicalTrials.gov · NCT07181109 (2026-03-31)
  8. SEC EDGAR · 0001178670 (2026-04-11)
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Upcoming Catalysts
vutrisiran (Amvuttra) — ATTR polyneuropathy sNDA
2026-05-22
13d ago
ALN-AGT — resistant hypertension
2027-05-05
in 335d
inclisiran (LEQVIO) — cardiovascular sNDA
2027-01-28
in 238d
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Clinical Trials
22
NCT03997383Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04153149Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04561518Transthyretin-Mediated Amyloidosis, ATTR Amyloidosis
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04883905Acute Hepatic Porphyria
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04982393Primary Hyperoxaluria Type 1
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05040373Hereditary Transthyretin-mediated (hATTR) Amyloidosis, Polyneuropathy
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05231785Early-Onset Alzheimer Disease
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06360289Hereditary Amyloidosis, Transthyretin-Related, Asymptomatic Carrier State
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06393712Cerebral Amyloid Angiopathy
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06585449Huntington's Disease
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06600321Advanced Hepatocellular Carcinoma, Metastatic Hepatocellular Carcinoma
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06659640Hereditary Hemorrhagic Telangiectasia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06679946Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06845202Obese or Overweight Healthy Volunteers, Type 2 Diabetes Mellitus (T2DM)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07052903Transthyretin Amyloidosis With Cardiomyopathy
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07181109High Risk Cardiovascular Disease, Hypertension, High Cardiovascular Risk
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07214727Alzheimer's Disease
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07223203Hereditary Transthyretin-Mediated Amyloidosis With Polyneuropathy, hATTR-PN
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07295717Healthy Volunteers
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07358078Transthyretin Amyloidosis With Cardiomyopathy
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07463846Obesity
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07465224Type 2 Diabetes Mellitus (T2DM)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
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Insider Activity
1
1 filing
Source ↗
sec_edgar · Retrieved 2026-04-11
Not financial advice. BiotechSigns profiles are AI-generated from verified public sources (ClinicalTrials.gov, SEC EDGAR) and are for informational purposes only. Always do your own due diligence before making investment decisions.
Score Breakdown
Score Trend
2026-04-132026-06-02
Signal Summary
PDUFA Dates3
Insider Filings1
Clinical Trials1
Sector Peers (RNAi Therapeutics)
ARWRArrowhead Pharmaceuticals
D
Data Provenance
cik1 verified
clinical trial22 verified
insider buy1 verified
trial count4 verified
Every claim backed by source URL from ClinicalTrials.gov or SEC EDGAR