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Ionis Pharmaceuticals

IONSAntisense Therapeutics
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Analyst Summary
✓ VERIFIED2026-04-11

Ionis Pharmaceuticals (IONS) is the lead sponsor of 20 active clinical trials listed on ClinicalTrials.gov[4], including 11 Phase 3[1], 4 Phase 2[2], 5 Phase 1[3].

Trial NCT05071300[5] evaluates Eplontersen in Hereditary Transthyretin-Mediated Amyloid Polyneuropathy with a target enrollment of 151 participants. Trial NCT06914609[6] evaluates ION582 in Angelman Syndrome with a target enrollment of 158 participants. Trial NCT05130450[7] evaluates Olezarsen in Familial Chylomicronemia Syndrome with a target enrollment of 60 participants.

IONS has 4 Form 4 insider filings recorded at the SEC in the past 30 days[8].

Sources

  1. ClinicalTrials.gov (2026-04-11)
  2. ClinicalTrials.gov (2026-04-11)
  3. ClinicalTrials.gov (2026-04-11)
  4. ClinicalTrials.gov (2026-04-11)
  5. ClinicalTrials.gov · NCT05071300 (2025-12-04)
  6. ClinicalTrials.gov · NCT06914609 (2026-04-08)
  7. ClinicalTrials.gov · NCT05130450 (2025-12-12)
  8. SEC EDGAR · 0000874015 (2026-04-11)
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Upcoming Catalysts
donidalorsen — hereditary angioedema
2026-06-25
in 21d
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Clinical Trials
20
NCT04136171Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04165486Multiple System Atrophy
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04768972Amyotrophic Lateral Sclerosis
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04849741Alexander Disease
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05071300Hereditary Transthyretin-Mediated Amyloid Polyneuropathy
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05127226Angelman Syndrome
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05130450Familial Chylomicronemia Syndrome
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05143957Phlebotomy Dependent Polycythemia Vera
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05185843Familial Chylomicronemia Syndrome
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05392114Hereditary Angioedema
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05659901Pelizaeus-Merzbacher Disease
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05667493Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05681351Severe Hypertriglyceridemia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06073574Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06073587Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06150716Pelizaeus-Merzbacher Disease
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06153966Prion Disease
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06430385Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06914609Angelman Syndrome
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07298447Hereditary Angioedema (HAE)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
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Insider Activity
1
4 filings
Source ↗
sec_edgar · Retrieved 2026-04-11
Not financial advice. BiotechSigns profiles are AI-generated from verified public sources (ClinicalTrials.gov, SEC EDGAR) and are for informational purposes only. Always do your own due diligence before making investment decisions.
Score Breakdown
Score Trend
2026-04-132026-06-02
Signal Summary
PDUFA Dates1
Insider Filings1
Clinical Trials5
Data Provenance
cik1 verified
clinical trial20 verified
insider buy1 verified
trial count4 verified
Every claim backed by source URL from ClinicalTrials.gov or SEC EDGAR