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Vertex Pharmaceuticals

VRTXGene Therapy
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Analyst Summary
✓ VERIFIED2026-04-11

Vertex Pharmaceuticals (VRTX) is the lead sponsor of 28 active clinical trials listed on ClinicalTrials.gov[4], including 16 Phase 3[1], 9 Phase 2[2], 7 Phase 1[3].

Trial NCT07204275[5] evaluates Povetacicept in Primary Membranous Nephropathy with a target enrollment of 176 participants. Trial NCT05331183[6] evaluates ELX/TEZ/IVA in Cystic Fibrosis with a target enrollment of 297 participants. Trial NCT04786262[7] evaluates VX-880 in Diabetes Mellitus, Type 1 with a target enrollment of 52 participants.

VRTX has 4 Form 4 insider filings recorded at the SEC in the past 30 days[8].

Sources

  1. ClinicalTrials.gov (2026-04-11)
  2. ClinicalTrials.gov (2026-04-11)
  3. ClinicalTrials.gov (2026-04-11)
  4. ClinicalTrials.gov (2026-04-11)
  5. ClinicalTrials.gov · NCT07204275 (2026-03-30)
  6. ClinicalTrials.gov · NCT05331183 (2026-01-21)
  7. ClinicalTrials.gov · NCT04786262 (2026-03-17)
  8. SEC EDGAR · 0000875320 (2026-04-11)
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Upcoming Catalysts
suzetrigine (VX-548) — moderate-to-severe acute pain sNDA
2026-06-20
in 16d
VX-147 — APOL1-mediated kidney disease
2027-02-12
in 253d
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Clinical Trials
28
NCT04208529Beta-Thalassemia, Thalassemia, Sickle Cell Disease, Hematologic Diseases, Hemoglobinopathies, Genetic Diseases, Inborn, Sickle Cell Anemia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04786262Diabetes Mellitus, Type 1, Impaired Hypoglycemic Awareness, Severe Hypoglycemia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05312879Proteinuric Kidney Disease
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05329649Sickle Cell Disease, Hydroxyurea Failure, Hydroxyurea Intolerance, Hemoglobinopathies, Hematological Diseases
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05331183Cystic Fibrosis
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05356195Beta-Thalassemia, Thalassemia, Genetic Diseases, Inborn, Hematologic Diseases, Hemoglobinopathies
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05422222Cystic Fibrosis
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05444257Cystic Fibrosis
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05477563Beta-Thalassemia, Thalassemia, Hematologic Diseases, Genetic Diseases, Inborn, Hemoglobinopathies, Sickle Cell Disease, Sickle Cell Anemia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05668741Cystic Fibrosis
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05791201Type 1 Diabetes
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05844449Cystic Fibrosis
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06154447Cystic Fibrosis
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06185764Myotonic Dystrophy Type 1 (DM1)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06460506Cystic Fibrosis
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06619860Diabetic Peripheral Neuropathic Pain
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06628908Diabetic Peripheral Neuropathic Pain
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06696443Diabetic Peripheral Neuropathic Pain
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06747572Autosomal Dominant Polycystic Kidney Disease (ADPKD)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06794996Proteinuric Kidney Disease
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06832410Type 1 Diabetes, Kidney Transplant
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06926621Myotonic Dystrophy Type 1 (DM1)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07161037Autosomal Dominant Polycystic Kidney Disease (ADPKD)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07204275Primary Membranous Nephropathy
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07231419Diabetic Peripheral Neuropathic Pain
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07283770Cystic Fibrosis
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07378865Pain
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07437105Cystic Fibrosis
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
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Insider Activity
1
4 filings
Source ↗
sec_edgar · Retrieved 2026-04-11
Not financial advice. BiotechSigns profiles are AI-generated from verified public sources (ClinicalTrials.gov, SEC EDGAR) and are for informational purposes only. Always do your own due diligence before making investment decisions.
Score Breakdown
Score Trend
2026-04-132026-06-02
Signal Summary
PDUFA Dates2
Insider Filings1
Clinical Trials1
Data Provenance
cik1 verified
clinical trial28 verified
insider buy1 verified
trial count4 verified
Every claim backed by source URL from ClinicalTrials.gov or SEC EDGAR