HomeTrialNCT03636438
🔬NCT03636438ACTIVE NOT RECRUITING

Long Term Follow Up to Evaluate DTX301 in Adults With Late-Onset OTC Deficiency

Study Summary

Determine the long-term safety of DTX301 following a single intravenous (IV) dose in adults with late-onset ornithine transcarbamylase (OTC) deficiency.

Interventions / Drugs
View on ClinicalTrials.gov ↗
Study Details
Enrollment11 participants
Primary Completion
Lead SponsorUltragenyx Pharmaceutical Inc
Data Retrieved2026-04-11 04:25:35.045605+00:00
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