HomeTrialNCT03989947
🔬NCT03989947Phase 2ACTIVE NOT RECRUITING

An Extension Study to Evaluate Safety and Efficacy of BMN 111 in Children With Achondroplasia

Study Summary

This is a Phase 2, open-label multi-center long-term extension study, with approximately 70 subjects, to evaluate the safety and efficacy of BMN111 in children with Achondroplasia until subjects reach near-adult final height. Eligible subjects will have completed 1 year of BMN111 or placebo treatment in the 111-206 study and once enrolled in the 111-208 extension study will receive a daily dose of BMN111 by subcutaneous injection according to their age as determined by 111-206.

Conditions
View on ClinicalTrials.gov ↗
Study Details
Enrollment73 participants
Primary Completion
Lead SponsorBioMarin Pharmaceutical
Data Retrieved2026-04-11 02:55:23.531561+00:00
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