HomeTrialNCT04153149
🔬NCT04153149Phase 3ACTIVE NOT RECRUITING

HELIOS-B: A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy

Study Summary

This study will evaluate the efficacy and safety of vutrisiran 25 mg administered subcutaneously (SC) once every 3 months (q3M) compared to placebo in participants with ATTR amyloidosis with cardiomyopathy.

View on ClinicalTrials.gov ↗
Study Details
Enrollment655 participants
Primary Completion
Lead SponsorAlnylam Pharmaceuticals
Data Retrieved2026-04-11 02:53:26.219343+00:00
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