HomeTrialNCT04281485
🔬NCT04281485Phase 3ACTIVE NOT RECRUITING

Study to Evaluate the Safety and Efficacy of PF-06939926 for the Treatment of Duchenne Muscular Dystrophy

Study Summary

The study will evaluate the safety and efficacy of gene therapy in boys with DMD. It is a randomized, double-blind, placebo-controlled study with two thirds of participants assigned to gene therapy. The one third of participants who are randomized to the placebo arm will have an opportunity for treatment with gene therapy at the beginning of the second year.

View on ClinicalTrials.gov ↗
Study Details
Enrollment114 participants
Primary Completion
Lead SponsorPfizer
Data Retrieved2026-04-11 02:55:53.189537+00:00
Not financial advice. BiotechSigns data is sourced from ClinicalTrials.gov, SEC EDGAR, and other public databases for research and informational purposes only. It does not constitute investment recommendations. Always do your own due diligence before making investment decisions.