HomeTrialNCT04580420
🔬NCT04580420Phase 2RECRUITING

Safety & Efficacy of DCR-PHXC in Patients With PH1 and ESRD

Study Summary

The aim of this study is to evaluate DCR-PHXC in participants with PH1 and severe renal impairment, with or without dialysis.

Interventions / Drugs
View on ClinicalTrials.gov ↗
Study Details
Enrollment28 participants
Primary Completion
Lead SponsorDicerna Pharmaceuticals, Inc., a Novo Nordisk company
Data Retrieved2026-04-11 02:55:47.366893+00:00
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