HomeTrialNCT04770753
🔬NCT04770753Phase 3ACTIVE NOT RECRUITING

A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Non-Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-NTDT)

Study Summary

The primary purpose of this study was to compare the effect of mitapivat versus placebo on hemolytic anemia in participants with alpha- or beta-non-transfusion dependent thalassemia (NTDT).

View on ClinicalTrials.gov ↗
Study Details
Enrollment194 participants
Primary Completion
Lead SponsorAgios Pharmaceuticals, Inc.
Data Retrieved2026-04-11 02:52:46.815024+00:00
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