HomeTrialNCT05270837
🔬NCT05270837Phase 3ACTIVE NOT RECRUITING

Study to Evaluate the Safety and Efficacy of Pegvaliase in Adolescents (Ages 12-17) With Phenylketonuria

Study Summary

This is a Phase 3 open-label randomized controlled study enrolling approximately 54 adolescents with PKU. The study is designed to assess the safety and efficacy of pegvaliase injections.

Interventions / Drugs
View on ClinicalTrials.gov ↗
Study Details
Enrollment55 participants
Primary Completion
Lead SponsorBioMarin Pharmaceutical
Data Retrieved2026-04-11 02:55:23.531438+00:00
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