HomeTrialNCT05331183
🔬NCT05331183Phase 3ACTIVE NOT RECRUITING

Study to Evaluate Elexacaftor/Tezacaftor/Ivacaftor (ELX/TEZ/IVA) Long-term Safety and Efficacy in Subjects Without F508del

Study Summary

This study will evaluate the long-term safety, efficacy and pharmacodynamics of ELX/TEZ/IVA in participants with cystic fibrosis (CF) with at least 1 non-F508del ELX/TEZ/IVA-responsive CF transmembrane conductance regulator (CFTR) gene mutation.

Conditions
Interventions / Drugs
View on ClinicalTrials.gov ↗
Study Details
Enrollment297 participants
Primary Completion
Lead SponsorVertex Pharmaceuticals Incorporated
Data Retrieved2026-04-11 02:55:58.035116+00:00
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