HomeTrialNCT05515536
🔬NCT05515536Phase 3ACTIVE NOT RECRUITING

A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia

Study Summary

The primary objective of this study is to assess the long-term safety of vatiquinone in participants with Friedreich ataxia (FA) previously exposed to vatiquinone.

Interventions / Drugs
View on ClinicalTrials.gov ↗
Study Details
Enrollment130 participants
Primary Completion
Lead SponsorPTC Therapeutics
Data Retrieved2026-04-11 04:25:04.378868+00:00
Not financial advice. BiotechSigns data is sourced from ClinicalTrials.gov, SEC EDGAR, and other public databases for research and informational purposes only. It does not constitute investment recommendations. Always do your own due diligence before making investment decisions.