HomeTrialNCT05693142
🔬NCT05693142Phase 2Phase 3RECRUITING

AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)

Study Summary

RGX-202 is a gene therapy designed to deliver a transgene for a novel microdystrophin that includes functional elements of naturally-occurring dystrophin including the C-Terminal (CT) domain. This is a multicenter, open-label dose evaluation clinical study to assess the safety, tolerability, and clinical efficacy of a one-time intravenous (IV) dose of RGX-202 in participants with Duchenne. For additional information on how to participate (or be considered for the study), please follow this link: https://mytomorro.ws/affinity-ct-gov

Interventions / Drugs
View on ClinicalTrials.gov ↗
Study Details
Enrollment65 participants
Primary Completion
Lead SponsorREGENXBIO Inc.
Data Retrieved2026-04-11 04:25:55.708134+00:00
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