Long-Term Follow-Up (LTFU) of Subjects Dosed With NTLA-2001

Study Summary

This is a follow-up study of subjects who received NTLA-2001 in a previous clinical trial as an observational evaluation of the long-term effects of the investigational therapy.

Conditions

Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy Wild-Type Transthyretin Cardiac Amyloidosis

Interventions / Drugs

View on ClinicalTrials.gov ↗

Sponsor

NTLA

Intellia Therapeutics

Gene Editing

D44/100

Study Details

Enrollment72 participants

Primary Completion—

Lead SponsorIntellia Therapeutics

Data Retrieved2026-04-11 04:23:01.073864+00:00

Not financial advice. BiotechSigns data is sourced from ClinicalTrials.gov, SEC EDGAR, and other public databases for research and informational purposes only. It does not constitute investment recommendations. Always do your own due diligence before making investment decisions.