HomeTrialNCT05769621
🔬NCT05769621RECRUITING

A Retrospective Study to Characterize Participants With Propionic Acidemia

Study Summary

This is a non-interventional, observational, global, multicenter, study describing participant characteristics, clinical outcomes, and event rates in participants with propionic acidemia (PA).

Interventions / Drugs
View on ClinicalTrials.gov ↗
Study Details
Enrollment60 participants
Primary Completion
Lead SponsorModernaTX, Inc.
Data Retrieved2026-04-11 02:55:38.209247+00:00
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