A Study of AAV5-hRKp.RPGR for the Treatment of Japanese Participants With X-linked Retinitis Pigmentosa

Study Summary

The purpose of the study is to assess the safety and tolerability of bilateral subretinal delivery of adeno-associated virus vector with a serotype 5 capsid human rhodopsin kinase promoter. retinitis pigmentosa guanosine triphosphatase regulator (AAV5-hRKp.RPGR).

Conditions

Retinitis Pigmentosa

Interventions / Drugs

AAV5-hRKp.RPGR AAV5-hRKp.RPGR

View on ClinicalTrials.gov ↗

Sponsor

Study Details

Enrollment4 participants

Primary Completion—

Lead SponsorJanssen Pharmaceutical K.K.

Data Retrieved2026-04-11 02:55:31.550816+00:00

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