A Phase 2 Study of Vosoritide in Children With Idiopathic Short Stature

Study Summary

The purpose of this study is to evaluate i) the effect of multiple doses of vosoritide and ii) the effect of the therapeutic dose of vosoritide compared to human growth hormone (hGH)(hGH; only in the United States), in children with idiopathic short stature (ISS).

Conditions

Idiopathic Short Stature

Interventions / Drugs

Vosoritide Injection Human Growth Hormone Placebo

View on ClinicalTrials.gov ↗

Sponsor

BMRN

BioMarin Pharmaceutical

Rare Disease

D36/100

Study Details

Enrollment100 participants

Primary Completion—

Lead SponsorBioMarin Pharmaceutical

Data Retrieved2026-04-11 02:55:23.531522+00:00

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