HomeTrialNCT07126262
🔬NCT07126262Phase 2RECRUITING

A Study of Vosoritide Versus Placebo in Children With Hypochondroplasia Aged 0 to < 36 Months

Study Summary

The purpose of this study is to evaluate the safety and efficacy of daily administration of vosoritide in participants with HCH aged 0 to \< 36 months over a 52-week period.

Interventions / Drugs
View on ClinicalTrials.gov ↗
Study Details
Enrollment60 participants
Primary Completion
Lead SponsorBioMarin Pharmaceutical
Data Retrieved2026-04-11 02:55:23.531530+00:00
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