HomeTrialNCT07455864
🔬NCT07455864RECRUITING

Lysosomal Acid Lipase Deficiency in Risk Groups

Study Summary

A multicenter real-world observational study of the prevalence, diagnostic pathways, and clinical characteristics of lysosomal acid lipase deficiency in pediatric and adolescent risk groups in the Russian Federation (HELIOS)

Interventions / Drugs
View on ClinicalTrials.gov ↗
Study Details
Enrollment1200 participants
Primary Completion
Lead SponsorAstraZeneca
Data Retrieved2026-04-11 02:55:19.910783+00:00
Not financial advice. BiotechSigns data is sourced from ClinicalTrials.gov, SEC EDGAR, and other public databases for research and informational purposes only. It does not constitute investment recommendations. Always do your own due diligence before making investment decisions.