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ProQR Therapeutics

PRQRRare Disease
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Analyst Summary
✓ VERIFIED2026-04-11

ProQR Therapeutics (PRQR) is the lead sponsor of 2 active clinical trials listed on ClinicalTrials.gov[4], including 1 Phase 3[1], 2 Phase 2[2], 1 Phase 1[3].

Trial NCT03913143[5] evaluates sepofarsen in Leber Congenital Amaurosis 10 with a target enrollment of 36 participants.

No Form 4 insider filings for PRQR were recorded at the SEC in the past 30 days[6].

Sources

  1. ClinicalTrials.gov (2026-04-11)
  2. ClinicalTrials.gov (2026-04-11)
  3. ClinicalTrials.gov (2026-04-11)
  4. ClinicalTrials.gov (2026-04-11)
  5. ClinicalTrials.gov · NCT03913143 (2022-03-17)
  6. SEC EDGAR · 0001612940 (2026-04-11)
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Clinical Trials
2
NCT03913143Leber Congenital Amaurosis 10, Blindness, Leber Congenital Amaurosis, Vision Disorders, Sensation Disorders, Neurologic Manifestations, Eye Diseases, Eye Diseases, Hereditary, Eye Disorders Congenital, Retinal Disease
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04123626Autosomal Dominant Retinitis Pigmentosa, Eye Diseases, Eye Diseases, Hereditary, Retinal Dystrophies, Retinal Disease, Retinitis, Vision Tunnel, Vision Disorders
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
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Insider Activity
1
0 filings
Source ↗
sec_edgar · Retrieved 2026-04-11
Not financial advice. BiotechSigns profiles are AI-generated from verified public sources (ClinicalTrials.gov, SEC EDGAR) and are for informational purposes only. Always do your own due diligence before making investment decisions.
Score Breakdown
Score Trend
2026-04-132026-06-02
Signal Summary
PDUFA Dates0
Insider Filings1
Clinical Trials1
Data Provenance
cik1 verified
clinical trial2 verified
insider buy1 verified
trial count4 verified
Every claim backed by source URL from ClinicalTrials.gov or SEC EDGAR