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BioMarin Pharmaceutical

BMRNRare Disease
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Analyst Summary
✓ VERIFIED2026-04-11

BioMarin Pharmaceutical (BMRN) is the lead sponsor of 25 active clinical trials listed on ClinicalTrials.gov[5], including 5 Phase 3[1], 10 Phase 2[2], 5 Phase 1[3], 1 Phase 4[4].

Trial NCT03424018[6] evaluates BMN 111 in Achondroplasia with a target enrollment of 119 participants. Trial NCT07073014[7] evaluates Vosoritide in Hypochondroplasia with a target enrollment of 140 participants. Trial NCT06224907[8] evaluates Valoctocogene roxaparvovec in Hemophilia A with a target enrollment of 6 participants.

BMRN has 11 Form 4 insider filings recorded at the SEC in the past 30 days[9].

Sources

  1. ClinicalTrials.gov (2026-04-11)
  2. ClinicalTrials.gov (2026-04-11)
  3. ClinicalTrials.gov (2026-04-11)
  4. ClinicalTrials.gov (2026-04-11)
  5. ClinicalTrials.gov (2026-04-11)
  6. ClinicalTrials.gov · NCT03424018 (2026-03-13)
  7. ClinicalTrials.gov · NCT07073014 (2025-07-18)
  8. ClinicalTrials.gov · NCT06224907 (2026-03-19)
  9. SEC EDGAR · 0001048477 (2026-04-11)
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Upcoming Catalysts
BMN 307 — phenylketonuria
2026-09-05
in 93d
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Clinical Trials
25
NCT02724228Achondroplasia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT03424018Achondroplasia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT03989947Achondroplasia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04476862Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04480567Phenylketonuria (PKU)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04554940Achondroplasia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT04684940Hemophilia A With Inhibitor, Hemophilia A With Anti Factor VIII
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05121376Hereditary Angioedema, HAE
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05270837Phenylketonuria (PKU)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05579548Phenylketonuria, Maternal
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05768386Hemophilia A
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT05813678Phenylketonuria (PKU)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06168201Achondroplasia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06212947Hypochondroplasia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06224907Hemophilia A
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06280209Duchenne Muscular Dystrophy
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06305234Phenylketonuria (PKU)
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06309979Idiopathic Short Stature
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06382155Idiopathic Short Stature
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06455059Hypochondroplasia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06668805Short Stature Homeobox- Containing Gene SHOX Deficiency, Noonan Syndrome, Turner Syndrome
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06738017Alpha 1-Antitrypsin Deficiency
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT06780332Phenylketonuria, PKU
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07073014Hypochondroplasia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
NCT07126262Hypochondroplasia
Source ↗
clinicaltrials_gov · Retrieved 2026-04-11
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Insider Activity
1
11 filings
Source ↗
sec_edgar · Retrieved 2026-04-11
Not financial advice. BiotechSigns profiles are AI-generated from verified public sources (ClinicalTrials.gov, SEC EDGAR) and are for informational purposes only. Always do your own due diligence before making investment decisions.
Score Breakdown
Score Trend
2026-04-132026-06-02
Signal Summary
PDUFA Dates1
Insider Filings1
Clinical Trials1
Data Provenance
cik1 verified
clinical trial25 verified
insider buy1 verified
trial count5 verified
Every claim backed by source URL from ClinicalTrials.gov or SEC EDGAR