Grades, scores, and FDA catalyst signals for Sleep Rare Disease stocks tracked by BiotechSign
| Ticker | Company | Score | Grade | Sector | Signals |
|---|---|---|---|---|---|
| AGIO | Agios Pharmaceuticals | 62 | C | Rare Disease | — |
| FOLD | Amicus Therapeutics | 57 | C | Rare Disease | — |
| INSM | Insmed Incorporated | 57 | C | Rare Disease | — |
| BCRX | BioCryst Pharmaceuticals | 56 | C | Rare Disease | — |
| PTCT | PTC Therapeutics | 55 | C | Rare Disease | — |
| BMRN | BioMarin Pharmaceutical | 53 | C | Rare Disease | — |
| RARE | Ultragenyx Pharmaceutical | 47 | D | Rare Disease | — |
| PHVS | Pharvaris NV | 37 | D | Rare Disease | — |
| PRQR | ProQR Therapeutics | 35 | F | Rare Disease | — |
| KNSA | Kiniksa Pharmaceuticals | 31 | F | Rare Disease | — |
| LRMR | Larimar Therapeutics | 29 | F | Rare Disease | — |
| STOK | Stoke Therapeutics | 29 | F | Rare Disease | — |
| DSGN | Design Therapeutics | 23 | F | Rare Disease | — |